Current Natural History Studies & Clinical Trials

Natural History Studies:

Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD) (GRASP-01-001)

Sponsor: Virginia Commonwealth University
Recruitment Status: Active

A Study of the Natural History of Patients With LGMD2E/R4, LGMD2D/R3, and LGMD2C/R5, ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice

Sponsor: Sarepta Therapeutics, Inc.
Recruitment Status: Active, Not Recruiting

Skeletal Muscle Biomarkers in People With Fragile Sarcolemmal Muscular Dystrophy

Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Recruitment Status: Active, Not Recruiting

There are no clinical trials available for LGMD2D patients at this time.

Past Clinical Trials

Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA

Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)

Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)

Sponsor: Dr. Jerry R. Mendell, Nationwide Children's Hospital

Recruitment Status: Completed

Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)

Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)

Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)

Sponsor: Nationwide Children's Hospital

Recruitment Status: Completed